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Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
Author(s):
Richard Finkel
,
Claudia A. Chiriboga
,
Jiri Vajsar
,
John Day
,
Jacqueline Montes
,
Darryl De Vivo
,
Mason Yamashita
,
Frank Rigo
,
Gene Hung
,
Eugene Schneider
,
Daniel A. Norris
,
Shuting Xia
,
C Frank Bennett
,
Kathie Bishop
Publication date:
2016-12-01
Journal:
The Lancet
Publisher:
Elsevier BV
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Journal for the Study of Indentureship and its Legacies
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Journal
DOI::
10.1016/S0140-6736(16)31408-8
License:
http://www.elsevier.com/tdm/userlicense/1.0/
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