ScienceOpen:
research and publishing network
For Publishers
Discovery
Metadata
Peer review
Hosting
Publishing
For Researchers
Join
Publish
Review
Collect
My ScienceOpen
Sign in
Register
Dashboard
Blog
About
Search
Advanced search
My ScienceOpen
Sign in
Register
Dashboard
Search
Search
Advanced search
For Publishers
Discovery
Metadata
Peer review
Hosting
Publishing
For Researchers
Join
Publish
Review
Collect
Blog
About
23
views
0
references
Top references
cited by
187
Cite as...
0 reviews
Review
0
comments
Comment
0
recommends
+1
Recommend
0
collections
Add to
0
shares
Share
Twitter
Sina Weibo
Facebook
Email
2,430
similar
All similar
Record
: found
Abstract
: not found
Article
: not found
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
Author(s):
Richard Finkel
,
Claudia A. Chiriboga
,
Jiri Vajsar
,
John Day
,
Jacqueline Montes
,
Darryl De Vivo
,
Mason Yamashita
,
Frank Rigo
,
Gene Hung
,
Eugene Schneider
,
Daniel A. Norris
,
Shuting Xia
,
C Frank Bennett
,
Kathie Bishop
Publication date:
2016-12-01
Journal:
The Lancet
Publisher:
Elsevier BV
Read this article at
ScienceOpen
Publisher
Cite as...
There is no author summary for this article yet. Authors can add summaries to their articles on ScienceOpen to make them more accessible to a non-specialist audience.
Related collections
NTT Journal for Theology and the Study of Religion
Author and article information
Journal
DOI::
10.1016/S0140-6736(16)31408-8
License:
http://www.elsevier.com/tdm/userlicense/1.0/
Data availability:
Comments
Comment on this article
Sign in to comment
scite_
Similar content
2,430
Expanded Access for Nusinersen in Patients With Spinal Muscular Atropy: Negotiating Limited Data, Limited Alternative Treatments, and Limited Hospital Resources.
Authors:
Holly Taylor
,
Benjamin S Wilfond
,
Christian Morales
PRO16 IMPROVED QUALITY OF LIFE FOR PATIENTS AND CAREGIVERS AMONG PATIENTS WITH LATER-ONSET SMA FOLLOWING TREATMENT WITH NUSINERSEN
Authors:
S. Zuluaga Sanchez
,
M Purser
,
G Mader
…
Spinal muscular atrophy: an integrated medical and pharmacy claims analysis of nusinersen uptake and gene therapy forecast among 15 million commercially insured
Authors:
C Starner
,
P Gleason
See all similar
Cited by
343
Advances in oligonucleotide drug delivery
Authors:
Thomas C Roberts
,
Robert (Bob) Langer
,
Matthew Wood
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Authors:
Richard Finkel
,
Eugenio Mercuri
,
Basil Darras
…
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
Authors:
Eugenio Mercuri
,
Basil Darras
,
Claudia A. Chiriboga
…
See all cited by
Version 1
Version 1