[1
] Neuromuscular Disorders Clinic, Department of Neurology, Vall d’Hebron University
Hospital, VHIR, European Reference Network on Rare, Neuromuscular Disorders (ERN EURO-NMD),
UAB, Barcelona, Spain;
[2
] Research and Development Department, SOM Biotech, S.L, Barcelona, Spain;
[3
] Pharmacy Department, Vall d’Hebron Research Institute (VHIR), Hospital Universitari
Vall d’Hebron, Barcelona, Spain;
[4
] Neuromuscular Disorders Unit, Neurology Department, Bellvitge University Hospital
– IDIBELL, Barcelona, Spain;
[5
] Department of Neurology, Neuromuscular Diseases Unit Hospital de la Santa Creu i
Sant Pau, Center for Networked Biomedical Research into Rare Diseases (CIBERER), UAB,
Barcelona, Spain