[1
]GRID grid.418640.f, Clinic for Special Children, ; Strasburg, PA USA
[2
]GRID grid.415783.c, ISNI 0000 0004 0418 2120, Penn Medicine-Lancaster General Hospital, ; Lancaster, PA USA
[3
]GRID grid.168645.8, ISNI 0000 0001 0742 0364, Departments of Pediatrics and Molecular, Cell & Cancer Biology, , University of Massachusetts School of Medicine, ; Worcester, MA USA
[4
]GRID grid.430417.5, ISNI 0000 0004 0640 6474, Department of Neurology, , Sydney Children’s Hospital Network, ; Sydney, New South Wales Australia
[5
]GRID grid.1005.4, ISNI 0000 0004 4902 0432, School of Clinical Medicine, , UNSW Medicine and Health, UNSW Sydney, ; Sydney, New South Wales Australia
[6
]GRID grid.83440.3b, ISNI 0000000121901201, The Dubowitz Neuromuscular Centre, , University College London, Great Ormond Street Institute of Child Health & Great Ormond
Street Hospital, ; London, UK
[7
]GRID grid.451056.3, ISNI 0000 0001 2116 3923, National Institute of Health Research, Great Ormond Street Hospital Biomedical Research
Centre, ; London, UK
[8
]GRID grid.410818.4, ISNI 0000 0001 0720 6587, Institute of Medical Genetics, , Tokyo Women’s Medical University, ; Tokyo, Japan
[9
]GRID grid.240344.5, ISNI 0000 0004 0392 3476, Center for Gene Therapy, , Nationwide Children’s Hospital, ; Columbus, OH USA
[10
]GRID grid.261331.4, ISNI 0000 0001 2285 7943, Department of Pediatrics and Department of Neurology, , The Ohio State University, ; Columbus, OH USA
[11
]Department of Paediatrics, MDUK Oxford Neuromuscular Centre, Oxford, UK
[12
]GRID grid.4861.b, ISNI 0000 0001 0805 7253, Neuromuscular Reference Center, Department of Pediatrics, , CHU & University of Liège, ; Liège, Belgium
[13
]Departments of Pediatrics, Neurology & Neurosurgery, Montreal Children’s Hospital,
McGill University Health Centre, Montreal, Quebec Canada
[14
]GRID grid.428618.1, ISNI 0000 0004 0456 3687, Department of Pediatrics, , Nemours Children’s Hospital, ; Orlando, FL USA
[15
]GRID grid.240871.8, ISNI 0000 0001 0224 711X, Center for Experimental Neurotherapeutics, St. Jude Children’s Research Hospital,
; Memphis, TN USA
[16
]GRID grid.32224.35, ISNI 0000 0004 0386 9924, Department of Neurology, , Massachusetts General Hospital, ; Boston, MA USA
[17
]GRID grid.14003.36, ISNI 0000 0001 2167 3675, Department of Neurology, , University of Wisconsin School of Medicine and Public Health, ; Madison, WI USA
[18
]GRID grid.4367.6, ISNI 0000 0001 2355 7002, Washington University School of Medicine, ; St. Louis, MO USA
[19
]GRID grid.239585.0, ISNI 0000 0001 2285 2675, Division of Pediatric Neurology, , Columbia University Medical Center, ; New York, NY USA
[20
]GRID grid.267313.2, ISNI 0000 0000 9482 7121, Department of Pediatrics, , University of Texas Southwestern Medical Center, ; Dallas, TX USA
[21
]GRID grid.413656.3, ISNI 0000 0004 0450 6121, Department of Neurology, , Helen DeVos Children’s Hospital, ; Grand Rapids, MI USA
[22
]GRID grid.430503.1, ISNI 0000 0001 0703 675X, Department of Pediatrics, , University of Colorado School of Medicine, ; Aurora, CO USA
[23
]GRID grid.19006.3e, ISNI 0000 0000 9632 6718, Department of Neurology, , David Geffen School of Medicine at UCLA, ; Los Angeles, CA USA
[24
]Novartis Gene Therapies, Inc., Bannockburn, IL USA
[25
]GRID grid.418424.f, ISNI 0000 0004 0439 2056, Translational Medicine, Novartis Institutes for BioMedical Research, ; Cambridge, MA USA
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