[1
]IRCCS, Ospedale Pediatrico Bambino Gesù Rome, Catholic University of the Sacred Heart,
Rome, Italy
[2
]University of Tübingen, Tübingen, Germany
[3
]University of Regensburg, Regensburg, Germany
[4
]BC Children’s Hospital, University of British Columbia, Vancouver, Canada
[5
]Imperial College Healthcare NHS Trust, St Mary’s Hospital, London, United Kingdom
[6
]The Hospital for Sick Children/University of Toronto, Toronto, Canada
[7
]Heinrich-Heine-University, Duesseldorf, Germany
[8
]Stanford University, Palo Alto, United States
[9
]Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, United States
[10
]Herbert Irving Comprehensive Cancer Center, Columbia University, New York, United
States
[11
]University College London Hospitals NHS Foundation Trust, London, United Kingdom
[12
]Children’s Hospital of Philadelphia, Philadelphia, United States
[13
]University of Milan, Milan, Italy
[14
]University of Athens, Athens, Greece
[15
]Joan and Sanford I Weill Medical College of Cornell University, New York, United States
[16
]Children’s Hospital of Philadelphia, Perelman School of Medicine at the University
of Pennsylvania, Philadelphia, United States
[17
]Vertex Pharmaceuticals Incorporated, Boston, United States
[18
]CRISPR Therapeutics, Cambridge, United States
[19
]Sarah Cannon Center for Blood Cancer at The Children’s Hospital at TriStar Centennial,
Nashville, United States
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