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Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector
Author(s):
Dawn E. Bowles
,
Scott McPhee
,
Chengwen Li
,
Steven J Gray
,
Jade J. Samulski
,
Angelique Camp
,
Juan Li
,
Bing Wang
,
Paul E Monahan
,
Joseph Rabinowitz
,
Joshua Grieger
,
Lakshmanan Govindasamy
,
Mavis Agbandje-McKenna
,
Xiao Xiao
,
R. Samulski
Publication date:
2012-02-01
Journal:
Molecular Therapy
Publisher:
Springer Nature
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Genome Engineering using CRISPR
Author and article information
Journal
DOI::
10.1038/mt.2011.237
PMC ID::
3277234
PubMed ID::
22068425
License:
http://creativecommons.org/licenses/by-nc-nd/4.0/
Data availability:
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