Journal ID (nlm-ta): PLoS One
Journal ID (iso-abbrev): PLoS ONE
Journal ID (publisher-id): plos
Journal ID (pmc): plosone
Title:
PLoS ONE
Publisher:
Public Library of Science
(San Francisco, CA USA
)
ISSN
(Electronic):
1932-6203
Publication date
(Electronic):
13
October
2016
Publication date Collection: 2016
Volume: 11
Issue: 10
Electronic Location Identifier: e0164684
Affiliations
[1
]University Hospitals Leuven, Child Neurology, Leuven, Belgium
[2
]Analysis Group, Inc., 111 Huntington Ave, 14
th floor, Boston, Massachusetts, United States of America
[3
]The Trajectory Analysis Project (TAP) Collaboration, One Broadway, 14
th floor, Cambridge, Massachusetts, United States of America
Cincinnati Children's Hospital Medical Center, UNITED STATES
Author notes
Competing Interests: JES, ES and JS are employees of Analysis Group, Inc., which received funding via the
Collaborative Trajectory Anlaysis Project (cTAP) for this research. This does not
alter our adherence to PLOS ONE policies on sharing data and materials.
-
Conceptualization: NG JaS.
-
-
Formal analysis: JaS ES JiS.
-
Funding acquisition: NG JaS.
-
-
Project administration: JaS.
-
Writing – original draft: NG JaS ES JiS.
-
Writing – review & editing: NG JaS ES JiS.
¶ Membership of the cTAP is provided in the Acknowledgments.
Article
Publisher ID:
PONE-D-16-23083
DOI: 10.1371/journal.pone.0164684
PMC ID: 5063281
PubMed ID: 27737016
SO-VID: d1d1820d-4e23-44f6-92e1-db8771c1486b
Copyright © © 2016 Goemans et al
License:
This is an open access article distributed under the terms of the
Creative Commons Attribution License, which permits unrestricted use, distribution, and reproduction in any medium, provided
the original author and source are credited.
Funded by: funder-id http://dx.doi.org/10.13039/100004319, Pfizer;
Funded by: Shire Pharmaceuticals
Funded by: funder-id http://dx.doi.org/10.13039/100008484, BioMarin Pharmaceutical;
Funded by: PTC Therapeutics
Funded by: Sarepta Therapeutics
Funded by: Fonds Spierzieke Kinderen
Award Recipient
:
Marleen vanden Hauwe
This study was co-funded by Biomarin, Pfizer, PTC Therapeutics, Sarepta Therapeutics,
and Shire as part of the Collaborative Trajectory Anlaysis Project (cTAP). MvdH received
funding for physical function testing from Fonds Spierzieke Kinderen. The study sponsors
were involved in the research design and review of the manuscript.
Subject:
Research Article
Subject:
Physical Sciences
Subject:
Chemistry
Subject:
Chemical Compounds
Subject:
Organic Compounds
Subject:
Steroids
Subject:
Physical Sciences
Subject:
Chemistry
Subject:
Organic Chemistry
Subject:
Organic Compounds
Subject:
Steroids
Subject:
Biology and Life Sciences
Subject:
Biomechanics
Subject:
Biological Locomotion
Subject:
Walking
Subject:
Biology and Life Sciences
Subject:
Physiology
Subject:
Biological Locomotion
Subject:
Walking
Subject:
Medicine and Health Sciences
Subject:
Physiology
Subject:
Biological Locomotion
Subject:
Walking
Subject:
Medicine and Health Sciences
Subject:
Diagnostic Medicine
Subject:
Prognosis
Subject:
Medicine and Health Sciences
Subject:
Neurology
Subject:
Muscular Dystrophies
Subject:
Duchenne Muscular Dystrophy
Subject:
Medicine and Health Sciences
Subject:
Clinical Genetics
Subject:
X-Linked Traits
Subject:
Duchenne Muscular Dystrophy
Subject:
Biology and Life Sciences
Subject:
Genetics
Subject:
Heredity
Subject:
Genetic Linkage
Subject:
Sex Linkage
Subject:
X-Linked Traits
Subject:
Duchenne Muscular Dystrophy
Subject:
Medicine and Health Sciences
Subject:
Epidemiology
Subject:
Natural History of Disease
Subject:
Medicine and Health Sciences
Subject:
Clinical Medicine
Subject:
Clinical Trials
Subject:
Medicine and Health Sciences
Subject:
Pharmacology
Subject:
Drug Research and Development
Subject:
Clinical Trials
Subject:
Research and Analysis Methods
Subject:
Clinical Trials
Subject:
Research and Analysis Methods
Subject:
Mathematical and Statistical Techniques
Subject:
Statistical Methods
Subject:
Forecasting
Subject:
Physical Sciences
Subject:
Mathematics
Subject:
Statistics (Mathematics)
Subject:
Statistical Methods
Subject:
Forecasting
Subject:
Biology and Life Sciences
Subject:
Biochemistry
Subject:
Proteins
Subject:
Cytoskeletal Proteins
Subject:
Dystrophin